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All Products Gene Editing AAVS1 Insertion Vectors

AAVS1 Insertion Vectors

Alstem offers two major types: reporter vectors (GFP, etc.) and customizable vectors for gene-of-interest expression. All cassettes include selectable markers and enable precise integration at the AAVS1 safe-harbor locus for stable, controlled expression using a shared gRNA/Cas9 vector.

Selection markers

  • Neomycin
  • Puromycin
  • Hygromycin

Promoters

  • Constitutive Expression
  • Inducible Expression

Versatile Applications

  • Reporter Expression
  • Custom Gene Expression

Mechanism

The AAVS1 CRISPR/Cas9 targeting system enables precise genome modifications through the homology-directed repair (HDR) pathway. The system combines a donor vector containing homology arms and selectable transgene cassettes—reporters like GFP/RFP or customizable genes-of-interest with constitutive or inducible promoters—with a separate gRNA/Cas9 expression vector. The gRNA guides Cas9 to the AAVS1 safe-harbor locus (PPP1R12C), where Cas9 introduces a double-strand break. The donor vector serves as a template for HDR, allowing stable, selectable integration of the transgene without disrupting endogenous gene expression. This controlled system supports overexpression, rescue studies, and functional analyses, providing a platform for insights into gene function disease mechanisms, and potential therapeutics.

AAVS1 Mechanism
Selection of Edited Cells

Selection of Edited Cells

Achieved via targeted insertion at the AAVS1 safe-harbor locus using a donor cassette containing an SA-T2A-antibiotic resistance gene, enabling stable, endogenous-level expression of the selectable marker to enrich cells with the targeted insertion.

Download System Guide

Application

Facilitates targeted insertion of genes or sequences at the AAVS1 safe-harbor locus, ensuring stable and predictable transgene expression.

Product List

ID Catalog# Name Unit Unit Price (USD) Actions
318 GA001 pSpCas9 nuclease & AAVS1 gRNA Vector10 μg at 0.5 μg/μL in TE $813.00 Add to Cart
319 AC2002 pAAVS1-SA-T2A-Neo-MCS Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
320 AC2301 pAAVS1-SA-T2A-Puro-CAG-MCS-SV40pA Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
321 AC2302 pAAVS1-SA-T2A-Neo-CAG-MCS-SV40pA Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
322 AC2303 pAAVS1-SA-T2A-HygR-CAG-MCS-SV40pA Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
323 AC2402 pAAVS1-SA-T2A-Neo-SV40pA-MCS-SFFV Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
324 AI3901 pAAVS1-SA-T2A-Puro-CAG-rtTA-SV40pA-TRE-MCS-SV40pA Donor Vector10 μg at 0.5 μg/μL in TE $1,351.00 Add to Cart
332 AC9311 pAAVS1-SA-T2A-Puro-CAG-EGFP-SV40pA Control Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
333 AC9321 pAAVS1-SA-T2A-Puro-CAG-copGFP-SV40pA Control Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
334 AC9411 pAAVS1-SA-T2A-Puro-SV40pA-EGFP-SFFV Control Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
335 AC9421 pAAVS1-SA-T2A-Puro-SV40pA-copGFP-SFFV Control Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
336 AC9312 pAAVS1-SA-T2A-Neo-CAG-EGFP-SV40pA Control Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
357 AI3903 pAAVS1-SA-T2A-HygR-CAG-rtTA-SV40pA-TRE-MCS-SV40pA Donor Vector10 μg at 0.5 μg/μL in TE $1,351.00 Add to Cart
379 AC7302 pAAVS1-SA-T2A-Neo-CAG-dCas9-KRAB-pA Donor Vector10 μg at 0.5 μg/μL in TE $1,244.00 Add to Cart
380 AC8302 pAAVS1-SA-T2A-Neo-CAG-dCas9-VPR-pA Donor Vector10 μg at 0.5 μg/μL in TE $1,244.00 Add to Cart
381 AC4411 pAAVS1-SA-T2A-Puro-CAG-EGFP-SV40pA-SV40pA-MCS-SFFV Donor Vector10 μg at 0.5 μg/μL in TE $1,027.00 Add to Cart
382 AI7902 pAAVS1-SA-T2A-Neo-CAG-rtTA-pA-TRE-dCas9-KRAB-pA Donor Vector10 μg at 0.5 μg/μL in TE $1,351.00 Add to Cart
383 AI8902 pAAVS1-SA-T2A-Neo-CAG-rtTA-SV40pA-TRE-dCas9-VPR-bGHpA Donor Vector10 μg at 0.5 μg/μL in TE $1,351.00 Add to Cart

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